The determination comes after recruitment and dosing in certain trials were paused after a young patient died due to acute ...

Columnist Patrick Moeschen, anticipating his own historic anniversary, celebrates champions of the disability rights movement ...

Lisa Littleton, who is the mother of two sons with Duchenne muscular dystrophy, one passed and one living, is a full-time caregiver. She describes the difficult balance between pushing for care and ...

Shalom Lim, who has Duchenne muscular dystrophy, shares how caregivers can support patient autonomy when it comes to ...

Hawkin Miller, who has Duchenne muscular dystrophy, shares motivation and advice for staying on track with treatment.

When living with Duchenne muscular dystrophy, taking a gamble feels better than not doing anything at all, columnist Betty Vertin writes.

We’ve only had a mental health — I wouldn’t call it a crisis — but where mental health really became an issue. And it was with my oldest son, and he was still middle school age. So I feel like, as a ...

DMD treatment KER-065 showed a good safety profile in a Phase 1 clinical trial with no serious side effects seen in healthy ...