Top-line Phase 3 trial data show ambulatory boys with Duchenne continued with motor improvements two years after a single ...
Columnist Shalom Lim is working with Julia Cameron's popular book "The Artist's Way" as a route to develop his creative self, ...
Columnist Robin Stemple has to make yet another adjustment due to FSHD, after a fall left him feeling "like an upside-down ...
As a parent and caregiver to three sons with DMD, columnist Betty Vertin's definition of what success looks like has changed over the years.
The FDA has granted fast track designation to DYNE-101, a therapy for myotonic dystrophy type 1 (DM1) now in testing in a ...
The U.S. Food and Drug Administration (FDA) has granted fast track designation to DYNE-101, a treatment candidate for myotonic dystrophy type 1 (DM1) — in which disease symptoms begin during adulthood ...
A pilot study in 19 LGMD patients and one with Becker MD found low-dose prednisone helped lower markers of muscle damage and ...