News

Sickle cell disease is the most common inherited blood disorder in the United States. According to the American Society of Hematology, approximately 70,000 to 100,000 people in the U.S. have SCD.
By facilitating affordable, accessible gene therapy for blood stem cells, this technology can transform the treatment landscape for genetic blood disorders, extending its benefits to a larger ...
This genetic blood disorder reduces the production of hemoglobin, the iron-containing protein in red blood cells carrying oxygen throughout the body. It can lead to severe anemia and may require ...
Woman with GATA2 primary immunodeficiency undergoes successful Bone Marrow Transplant at private hospital, overcoming rare ...
Individuals with a genetic predisposition to Alzheimer’s disease show altered blood levels indicating damaged neuronal contacts as early as 11 years before the expected onset of dementia symptoms.
Children's Hospital of Michigan announced Monday that it now is treating the first person in Michigan — a teenage boy — with a newly approved gene therapy for the rare inherited blood disorder ...