Adeno-associated virus (AAV)–mediated gene therapy was one of the focal points of this year's Muscular Dystrophy Association conference. Here, Barry Byrne, MD, PhD, University of Florida, speaks to ...
In a preclinical study, researchers at Children's Hospital of Philadelphia (CHOP) demonstrated a novel gene therapy with ...
After scoring tax abatements for a $100 million investment in The Woodlands last year, the company appears to be close to beginning the project.
The future of medicine is being shaped by a confluence of factors at play. If there are worries galore around drug resistant ...
Using an unbiased approach, this important study discovered a role of Ezh2 in the differentiation of granule neuron precursors, the cell of origin for Shh group of medulloblastoma. Furthermore, the ...
Johns Hopkins Medicine laboratory scientists say they have developed a potential new way to treat a variety of rare genetic ...
Pancreatic cancer’s deadly resilience may be tied to extrachromosomal DNA, which allows tumor cells to rapidly adapt to ...
The Times of Israel on MSN2d
Israeli researchers use gene editing to eliminate 50% of head and neck tumorsTel Aviv University scientists say that they can inject CRISPR genetic 'molecular scissors' to shrink tumors by 90%; ...
Sarepta Therapeutics said on Tuesday a young man has died due to acute liver failure after treatment with its gene therapy for a rare muscular dystrophy.
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