Sebastien Beauzile, 21, is the first New Yorker to have received the breakthrough Lyfgenia treatment, according to the New ...

Now, thanks to a groundbreaking genetic treatment ... cell disease in which there is homozygosity for the mutation that causes HbS. Sickle-cell anaemia is also referred to as "HbSS", "SS disease ...

The new gene therapies for sickle cell disease ... cell disease in which there is homozygosity for the mutation that causes HbS. Sickle-cell anaemia is also referred to as "HbSS", "SS disease ...

Scientists have discovered more than a dozen genes that regulate the production of fetal hemoglobin in people of African ...

The field of gene editing recently got a major boost from Massachusetts-based Beam Therapeutics, and the company’s Durham ...

A person who has sickle cell disease has inherited a mutation (sickle allele) from each parent and is homozygous for this mutation in gene function. *Definitions from GeneClinics ™ Glossary (see ...

Sickle cell disease stems from a mutation in the gene that makes hemoglobin, the protein in red blood cells that carries oxygen throughout the body. Orkin’s team and others revealed that ...

Scientists from Johns Hopkins Medicine and eight other institutions in the United States, Africa and Europe say they have identified a potential new gene target that could be edited to treat sickle ...