Q4 2024 Earnings Call Transcript February 13, 2025 Operator: Good morning, and welcome to Agios’ Fourth Quarter 2024 ...
Dependency on future regulatory approvals for PYRUKYND and potential launches in thalassemia ... sickle cell disease, pediatric PK deficiency, myelodysplastic syndromes (MDS)-associated anemia ...
According to research studies and demographic surveys by the Union Ministry of Tribal Affairs and genetic researchers, sickle cell disease is widespread in many tribal groups of India, especially amon ...
Despite promising Phase 3 results, safety concerns, namely liver injury, have impacted Agios stock and could affect Pyrukund's approval and market adoption. Read the full report here.
Kyle Registre's childhood dream of becoming a pilot can finally come true now that he says he's been cured of sickle cell ...
With the addition of Casgevy, Children’s Hospital Los Angeles now offers two gene therapies for sickle cell, the first being Lyfgenia.